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Rational Design of Short Locked Nucleic Acid-Modified 2- O -Methyl Antisense Oligonucleotides for Efficient Exon-Skipping In Vitro



Rational Design of Short Locked Nucleic Acid-Modified 2- O -Methyl Antisense Oligonucleotides for Efficient Exon-Skipping In Vitro



Molecular Therapy — Nucleic Acids 9: 155-161




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Accession: 065040738

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DOI: 10.1016/j.omtn.2017.09.002


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